Combining Translation Readthrough Inducing Drugs and Nonsense Mediated Decay Pathway Inhibition to Rescue of CFTRW1282X in Cystic Fibrosis Cell Model System


Cellular system | 2024

Roberta Bongiorno, Emanuele Vitale, Davide Ricci, Pietro Salvatore Carollo, Ivana Pibiri, Raffaella Melfi, Andrea Pace, Laura Lentini